A Cost-Utility Analysis Of Vertex's CF Drugs — What It Teaches Us About Trial Design
Cystic fibrosis transmembrane conductance regulator (CFTR) modulators have differential effects on cystic fibrosis macrophage function | Scientific Reports
Cystic fibrosis transmembrane conductance regulator modulators: precision medicine in cystic fibrosis. - Abstract - Europe PMC
Vertex to Present New Data at European and North American Virtual Cystic Fibrosis Conferences Highlighting Long-Term Use of CFTR Modulators | Business Wire
Frontiers | CFTR Modulators: The Changing Face of Cystic Fibrosis in the Era of Precision Medicine
FAQs — CF Buyers Club
Emerging Cystic Fibrosis Transmembrane Conductance Regulator Modulators as New Drugs for Cystic Fibrosis: A Portrait of in Vitro Pharmacology and Clinical Translation | ACS Pharmacology & Translational Science
Modulator therapies for cystic fibrosis - ScienceDirect
Cystic Fibrosis awareness — WindroseCG
Vertex backed for continued cystic fibrosis dominance with Trikafta replacement in good shape
Vertex's CFTR Modulators Too Costly, ICER Panel Says; Vertex Disagrees
Vertex to Present Data Demonstrating Significant Benefits of Long-Term and Early Treatment With CFTR Modulators at the European Cystic Fibrosis Conference | Business Wire
Frontiers | CFTR Modulators: The Changing Face of Cystic Fibrosis in the Era of Precision Medicine
Towards next generation therapies for cystic fibrosis: Folding, function and pharmacology of CFTR - ScienceDirect
Chemical structures of CFTR modulators discussed in the paper.... | Download Scientific Diagram
ACPCF on Twitter: "Invitation for a Vertex webinar: 'Hot topics in the management of patients with cystic fibrosis treated with CFTR modulators' 🗓 Wednesday 10 November 2021 🕐13:00–14:00 BST To register: https://t.co/jwhSUqPcur
Vertex Pharmaceuticals: Humanizing drug discovery
Vertex to Initiate Phase 3 Development Program for New Once-Daily Triple Combination Regimen in People With Cystic Fibrosis | Business Wire
Overview of CFTR Modulators and Gene Therapy | IntechOpen
ADDING MULTIMEDIA FDA Approves TRIKAFTA (elexacaftor/tezacaftor/ivacaftor and ivacaftor) to Treat the Underlying Cause of Cystic Fibrosis in People Ages 12 and Older Who Have at Least One F508del Mutation | Business Wire
Impact of CFTR modulator use on outcomes in people with severe cystic fibrosis lung disease | European Respiratory Society
NHS England and Vertex announce agreement for cystic fibrosis medicines
Chemical structure of several CF transmembrane conductance regulator... | Download Scientific Diagram
Genes | Free Full-Text | Transcriptomic and Proteostasis Networks of CFTR and the Development of Small Molecule Modulators for the Treatment of Cystic Fibrosis Lung Disease