Gene therapy for cystic fibrosis: new tools for precision medicine | Journal of Translational Medicine | Full Text
Overview of CFTR Modulators and Gene Therapy | IntechOpen
How to determine the mechanism of action of CFTR modulator compounds: A gateway to theranostics - ScienceDirect
Personalized medicine in CF: from modulator development to therapy for cystic fibrosis patients with rare CFTR mutations | American Journal of Physiology-Lung Cellular and Molecular Physiology
IJMS | Free Full-Text | The Effect of CFTR Modulators on Airway Infection in Cystic Fibrosis
Modulator therapies for cystic fibrosis - ScienceDirect
Frontiers | CFTR Modulators: Shedding Light on Precision Medicine for Cystic Fibrosis
Therapeutic approaches to CFTR dysfunction: From discovery to drug development - ScienceDirect
A new era for people with cystic fibrosis | SpringerLink
Cystic fibrosis transmembrane conductance regulator modulators for cystic fibrosis: a new dawn? | Archives of Disease in Childhood
Frontiers | CFTR Modulators: The Changing Face of Cystic Fibrosis in the Era of Precision Medicine
Triple combination therapy for cystic fibrosis is here!
New drugs in cystic fibrosis: what has changed in the last decade? - Juliana Roda, Catarina Pinto-Silva, Iris A.I. Silva, Carla Maia, Susana Almeida, Ricardo Ferreira, Guiomar Oliveira, 2022
IJMS | Free Full-Text | Dysfunctional Inflammation in Cystic Fibrosis Airways: From Mechanisms to Novel Therapeutic Approaches
CFTR Modulator Therapies | Cystic Fibrosis Foundation
Cystic fibrosis transmembrane conductance regulator modulators: precision medicine in cystic fibrosis. - Abstract - Europe PMC
Pulmonary Insights | Miracle Drugs for Cystic Fibrosis Are Here, with More to Come | Pulmonary Insights
Perspectives on the translation of in-vitro studies to precision medicine in Cystic Fibrosis - eBioMedicine
Potential effects of CFTR modulators on inflammation and host responses... | Download Scientific Diagram
Frontiers | Emerging Therapeutic Approaches for Cystic Fibrosis. From Gene Editing to Personalized Medicine
Types of CFTR Modulators for CF: Correctors, Potentiators, and Amplifiers
Cureus | A Review of Trikafta: Triple Cystic Fibrosis Transmembrane Conductance Regulator (CFTR) Modulator Therapy | Article
Site of action of the different CFTR modulator drugs. CFTR modulator... | Download Scientific Diagram
Combination therapy in Phe508del CFTR: how many will be enough?
Cells | Free Full-Text | Therapeutic Approaches for Patients with Cystic Fibrosis Not Eligible for Current CFTR Modulators
Modulators of CFTR. Updates on clinical development and future directions - ScienceDirect
Triple combination therapy for cystic fibrosis is here!
CFTR corrector (1) and potentiator (2) modulators work together to... | Download Scientific Diagram