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Gene therapy for cystic fibrosis: new tools for precision medicine |  Journal of Translational Medicine | Full Text
Gene therapy for cystic fibrosis: new tools for precision medicine | Journal of Translational Medicine | Full Text

Overview of CFTR Modulators and Gene Therapy | IntechOpen
Overview of CFTR Modulators and Gene Therapy | IntechOpen

How to determine the mechanism of action of CFTR modulator compounds: A  gateway to theranostics - ScienceDirect
How to determine the mechanism of action of CFTR modulator compounds: A gateway to theranostics - ScienceDirect

Personalized medicine in CF: from modulator development to therapy for cystic  fibrosis patients with rare CFTR mutations | American Journal of  Physiology-Lung Cellular and Molecular Physiology
Personalized medicine in CF: from modulator development to therapy for cystic fibrosis patients with rare CFTR mutations | American Journal of Physiology-Lung Cellular and Molecular Physiology

IJMS | Free Full-Text | The Effect of CFTR Modulators on Airway Infection  in Cystic Fibrosis
IJMS | Free Full-Text | The Effect of CFTR Modulators on Airway Infection in Cystic Fibrosis

Modulator therapies for cystic fibrosis - ScienceDirect
Modulator therapies for cystic fibrosis - ScienceDirect

Frontiers | CFTR Modulators: Shedding Light on Precision Medicine for Cystic  Fibrosis
Frontiers | CFTR Modulators: Shedding Light on Precision Medicine for Cystic Fibrosis

Therapeutic approaches to CFTR dysfunction: From discovery to drug  development - ScienceDirect
Therapeutic approaches to CFTR dysfunction: From discovery to drug development - ScienceDirect

A new era for people with cystic fibrosis | SpringerLink
A new era for people with cystic fibrosis | SpringerLink

Cystic fibrosis transmembrane conductance regulator modulators for cystic  fibrosis: a new dawn? | Archives of Disease in Childhood
Cystic fibrosis transmembrane conductance regulator modulators for cystic fibrosis: a new dawn? | Archives of Disease in Childhood

Frontiers | CFTR Modulators: The Changing Face of Cystic Fibrosis in the  Era of Precision Medicine
Frontiers | CFTR Modulators: The Changing Face of Cystic Fibrosis in the Era of Precision Medicine

Triple combination therapy for cystic fibrosis is here!
Triple combination therapy for cystic fibrosis is here!

New drugs in cystic fibrosis: what has changed in the last decade? -  Juliana Roda, Catarina Pinto-Silva, Iris A.I. Silva, Carla Maia, Susana  Almeida, Ricardo Ferreira, Guiomar Oliveira, 2022
New drugs in cystic fibrosis: what has changed in the last decade? - Juliana Roda, Catarina Pinto-Silva, Iris A.I. Silva, Carla Maia, Susana Almeida, Ricardo Ferreira, Guiomar Oliveira, 2022

IJMS | Free Full-Text | Dysfunctional Inflammation in Cystic Fibrosis  Airways: From Mechanisms to Novel Therapeutic Approaches
IJMS | Free Full-Text | Dysfunctional Inflammation in Cystic Fibrosis Airways: From Mechanisms to Novel Therapeutic Approaches

CFTR Modulator Therapies | Cystic Fibrosis Foundation
CFTR Modulator Therapies | Cystic Fibrosis Foundation

Cystic fibrosis transmembrane conductance regulator modulators: precision  medicine in cystic fibrosis. - Abstract - Europe PMC
Cystic fibrosis transmembrane conductance regulator modulators: precision medicine in cystic fibrosis. - Abstract - Europe PMC

Pulmonary Insights | Miracle Drugs for Cystic Fibrosis Are Here, with More  to Come | Pulmonary Insights
Pulmonary Insights | Miracle Drugs for Cystic Fibrosis Are Here, with More to Come | Pulmonary Insights

Perspectives on the translation of in-vitro studies to precision medicine  in Cystic Fibrosis - eBioMedicine
Perspectives on the translation of in-vitro studies to precision medicine in Cystic Fibrosis - eBioMedicine

Potential effects of CFTR modulators on inflammation and host responses...  | Download Scientific Diagram
Potential effects of CFTR modulators on inflammation and host responses... | Download Scientific Diagram

Frontiers | Emerging Therapeutic Approaches for Cystic Fibrosis. From Gene  Editing to Personalized Medicine
Frontiers | Emerging Therapeutic Approaches for Cystic Fibrosis. From Gene Editing to Personalized Medicine

Types of CFTR Modulators for CF: Correctors, Potentiators, and Amplifiers
Types of CFTR Modulators for CF: Correctors, Potentiators, and Amplifiers

Cureus | A Review of Trikafta: Triple Cystic Fibrosis Transmembrane  Conductance Regulator (CFTR) Modulator Therapy | Article
Cureus | A Review of Trikafta: Triple Cystic Fibrosis Transmembrane Conductance Regulator (CFTR) Modulator Therapy | Article

Site of action of the different CFTR modulator drugs. CFTR modulator... |  Download Scientific Diagram
Site of action of the different CFTR modulator drugs. CFTR modulator... | Download Scientific Diagram

Combination therapy in Phe508del CFTR: how many will be enough?
Combination therapy in Phe508del CFTR: how many will be enough?

Cells | Free Full-Text | Therapeutic Approaches for Patients with Cystic  Fibrosis Not Eligible for Current CFTR Modulators
Cells | Free Full-Text | Therapeutic Approaches for Patients with Cystic Fibrosis Not Eligible for Current CFTR Modulators

Modulators of CFTR. Updates on clinical development and future directions -  ScienceDirect
Modulators of CFTR. Updates on clinical development and future directions - ScienceDirect

Triple combination therapy for cystic fibrosis is here!
Triple combination therapy for cystic fibrosis is here!

CFTR corrector (1) and potentiator (2) modulators work together to... |  Download Scientific Diagram
CFTR corrector (1) and potentiator (2) modulators work together to... | Download Scientific Diagram